I'm fighting a fatal disease that took the life of my brother. I work in biotech and know there are medical advances that ...

A 12-year-old boy with a severe form of muscular dystrophy has said it is "cruel" that a new drug is not being made available ...

Medically reviewed by Smita Patel, DO Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed ...

Caleb Kasner and his brother Duncan Kasner move around a little differently than average kids. The two brothers have Duchenne ...

Young boy with severe form of muscular dystrophy says it is 'cruel' that a new drug is not being made available in NI ...

Families and doctors spoke out against the cuts at a roundtable at the UMass Chan Medical School in Worcester, Massachusetts.

Solid said that the first patients to receive its Duchenne gene therapy all produced high levels of the target protein, an ...

Entrada Therapeutics' innovative Endosomal Escape Vehicle platform, poised to revolutionize drug delivery. Click here to read ...

Telangana's Chief Minister, Revanth Reddy, has intervened to assist Rakesh, a student afflicted with Pseudo Muscular ...

Chief Minister A Revanth Reddy was moved by the miserable condition of a young student, Rakesh, who has been suffering from a ...